Senior Director, Global Medical Expert Gene Therapies

Why Join UsBe a hero for our rare disease patientsAt Ultragenyx we fundamentally believe that taking real impactful action to care for the needs of patients and our people is always the right thing to achieve this goal our vision is to lead the future of rare disease medicine. For us this means going where other biopharma companies wont go challenging the status quo and creating a new model that advances our field so more patients and caregivers can benefit from life-changing treatments. We do this by following the science applying a novel rapid development approach making innovative medicines at fair and reasonable prices and creating a collaborative ecosystem to reach patients in ways that are most meaningful for them.Our commitment and care for patients extends to our people so culture is an essential cornerstone for Ultragenyx. We remain continuously focused on creating a supportive and inclusive environment of profound learning and growth so employees can thrive in all areas of their lives in and outside of we want to be an organization where we would be proud for our family friends and children to work.If you want to have a meaningful impact do the best work of your career and grow a lot both professionally andpersonally come join our team.

Position Summary:

ultracurious Apply your biggest ideas in courageous ways

Ultragenyx isseekinga dynamic and experienced physician tojoin thehigh-profile and innovativeGene Therapy TreatmentTeamin EMEA(Europe MiddleEastand Africa).Thephysicianwill play a keymedicalaffairsleadershiprole within the gene therapy portfolio initially focused onMucopolysaccharidosis TypeIIIAandGlycogen Storage Disease Type position will beinstrumental inensuring scientifically rigorous compliant and effective implementation of one-time gene therapiesin EMEAthrough both pre-approvalmanagedaccess programs and post-approvalcommercial treatment.

Located in EMEA and reporting to theU.S. basedVP Global Medical Expert(GME) Gene TherapiestheSenior Directorwill partner closely withtheEMEA and U.S Medicalteamsas well asClinical DevelopmentSafety CMC and Commercial leadershipto facilitate medical access and enable treatment of patients with gene therapies.

The role requires extensive peer-to-peer interactions withexternal physiciansproviding gene therapy treatmenttoenable successfulmedical onboarding of treating sites whilealso leading education and scientific exchangeonsafetyefficacy patientmanagement including immunomodulation successful candidate will becomfortable working in a fast-paced intellectual environmentleverage their direct experience in patient care and gene therapyandcanworkeffectivelyat the interface between clinical development and medical affairsboth regionally and globallyleveraging their expertise to advance our mission to change the future of rare disease medicine.

Work Model:

Flex: This role will typically require onsite work 2-3 days each week or more depending on business many locations the business will set certain days each week that Flex employees are required to be onsite.

Responsibilities:

• Serve asasenior external medical leader for Ultragenyx gene therapies leading compliant complex scientific discussions with treating physiciansin EMEA
• Enablesuccessful implementation of gene therapiesin EMEAboth within Ultragenyx and with external medical experts
• Respond to inquiries and questions from treating sitesin EMEAwithappropriate levelof urgency
• Leadthestrategic and scientificdevelopment ofeducational materials andtrainingfor the gene therapy treatment centersin EMEAto ensure those centers are well prepared to manage patients throughout their gene therapy treatment journey
• Provideexpertiseand contribute as neededtocountry-level regulatoryagencysubmissionsanddata generation initiatives
• Advise on strategic development of publications and medical materials thatenableexternal medicalengagementandaddressevidence gaps toinformclinicaldecision making
• Work in partnership with VPGME Gene TherapiesandEMEA RegionalMedicalAffairsLeadsto develop and implementtheEMEAGene Therapies Treatment Team Framework
• Lead education initiatives for the broaderEMEAregional medical affairs and cross functional teams preparing or potentialgene therapy launches
• Represent Ultragenyx at key scientific and external stakeholder meetings to advance awareness and deep understanding of our science and therapies
• Stay abreast of internal and external developments trends and dynamics and provide direction for strategic implications to the development and commercialization of gene therapy

Requirements:

• Medical Doctor(MDMBBSor equivalent withPhD preferred) withsubspecialtytraining and certificationin Clinical Immunology Clinical/Biochemical Genetics Rheumatology or Neurology (required)
• Academic/Faculty experience(5years)witha track recordof high-quality publications
• Pharmaceutical experience in drug development and clinical trials or Medical Affairs (3years)
• Experiencein the management of patients receiving systemic AAV gene therapyin the clinical trialand/orpostregulatory authorityapproval setting
• Demonstrated ability to prioritize and lead complex postapproval gene therapy activities applying sound scientific judgment while enabling crossfunctional decisionmaking
• Demonstrated ability to lead through ambiguity and make strategic medical decisions in firstor bestinclass therapeutic settings
• Demonstrated success working in a cross functional or multidisciplinary settingisessential
• An established broad network of key experts and leaders within the rare disease community
• Travel:Estimated at25%-35%but may reduce with time as launches progress and team grows

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Full Time employees across the globe enjoy a range of benefits including but not limited to: Generous vacation time and public holidays observed by the company Volunteer days Long term incentive and Employee stock purchase plans or equivalent offerings Employee wellbeing benefits Fitness reimbursement Tuition sponsoring Professional development plans* Benefits vary by region and country

Ultragenyx Pharmaceutical is an equal opportunity employer and prohibits unlawful discrimination based on race color religion gender sexual orientation gender identity/expression national origin/ancestry age disability marital and veteran status and any other status or classification protected by applicable federal state and/or local laws. Reasonable accommodation will be provided for all protected statuses or classifications protected by applicable law including individuals with disabilities disabled veterans for pregnancy childbirth and related medical conditions and based on sincerely held religious beliefs. Applicants can request an accommodation prior to accepting a job offer. If you require reasonable accommodation in completing this application or in any part of the recruitment process you may contact Talent Acquisition by emailing us at .

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Required Experience:

Exec

Employment Type : Full Time
Experience: years
Vacancy: 1